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Ultragenyx Pharmaceutical Inc

RARE
Healthcare|Biotechnology|USA
$33.82
-0.81 (-2.34%)

About

Ultragenyx Pharmaceutical Inc is a USA-based biopharmaceutical company. The company identifies, acquires, develops, and commercializes novel products for the treatment of serious, rare, and ultra-rare diseases, with a focus on debilitating genetic conditions. Its medicine portfolio includes Crysvita, Dojolvi, and Mepsevii. Crysvita is indicated for the treatment of X-linked hypophosphatemia (XLH) in adult and pediatric patients aged one year and older. Mepsevii is indicated for pediatric and adult patients for the treatment of Mucopolysaccharidosis VII. The company operates across North America, Latin America, Europe, the Middle East and Africa, and Asia-Pacific, with the majority of its revenue generated from North America.

Stock Price

+9.0%(1Y)

Pipeline Summary

90 total trials
14
Phase 1
41
Phase 2
17
Phase 3
1
Phase 4
Terminated: 13Completed: 41Active: 12Unknown: 4NO_LONGER_AVAILABLE: 3AVAILABLE: 2Recruiting: 6ENROLLING_BY_INVITATION: 4NOT_YET_RECRUITING: 1Withdrawn: 4

Active Trials (18)

Setrusumab vs Placebo for Osteogenesis Imperfecta
NCT05125809Osteogenesis Imperfecta
Phase 2Phase 3Active
Enrollment: 183 participants
A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease
NCT04884815Wilson Disease
Phase 1Phase 2Active
Enrollment: 82 participants
Setrusumab in Pediatric Japanese Subjects With Osteogenesis Imperfecta
NCT06636071Osteogenesis Imperfecta
Phase 3Active
Enrollment: 6 participants
Tumor-induced Osteomalacia Disease Monitoring Program
NCT04783428Tumor-induced Osteomalacia (TIO)
Active
Enrollment: 23 participants
A Study to Determine the Effect of Triheptanoin Compared With Even-Chain MCT on MCEs in Pediatric Patients With LC-FAOD
NCT05933200Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
Phase 3Active
Enrollment: 69 participants
View all 18 active trials →

BioScore

5.6/10
Watchlist

Ownership

Recent Insider Trades

Horn HowardSELL
2026-07-014,698 shares @ $33.13
Sanders Corazon (Corsee) D.SELL
2026-06-152,000 shares @ $25.05
Parschauer Karah HerdmanSELL
2026-06-151,899 shares @ $24.62
Horn HowardSELL
2026-06-014,653 shares @ $23.77
SULIMAN SHEHNAAZSELL
2026-05-185,740 shares @ $25.12

Recent News

2026-07-07 16:35:16
2026-06-16 00:02:03
Data last updated: Jul 12, 2026, 07:30 PM