Rocket Pharmaceuticals Inc
RCKTHealthcare|Biotechnology|USA
$3.91
-0.28 (-6.68%)
Tangible Book
$1.59
Earnings Power
$0.30
Clinical Trials (37)
| Trial | Conditions | Phase | Status | Enrollment | Design | Drug |
|---|---|---|---|---|---|---|
| NCT07209787 SIS-Reinforced vs. Conventional Anastomosis for Mid-to-Low Rectal Cancer: A Multicenter RCT on Anastomotic Leak | Rectal Cancer | P4 | Recruiting | 966 | RCT, Open-label | — |
| NCT06312982 A Series of Neoadjuvant Chemoradiotherapy Combined With Immunotherapy for Locally Advanced Rectal Cancer | Locally Advanced Rectal Carcinoma | P2P3 | Recruiting | 375 | RCT, Single-blind | Tislelizumab |
| NCT06092034 A Gene Therapy Study of RP-A501 in Male Patients With Danon Disease | Danon Disease | P2 | Recruiting | 14 | Open-label | — |
| NCT04248439 Gene Therapy for Fanconi Anemia, Complementation Group A | Fanconi Anemia Complementation Group A | P2 | Active | 5 | Open-label | RP-L102 |
| NCT07137338 A Phase 1 AAV Gene Therapy Trial Evaluating Safety and Preliminary Efficacy of RP-A701 in Subjects With BAG3 Dilated Cardiomyopathy | Dilated Cardiomyopathy (DCM) | P1 | Recruiting | 8 | Open-label | — |
| NCT05885412 A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM) | PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM) | P1 | Recruiting | 9 | Open-label | — |
| NCT06644742 PKP2-ACM Natural History Study | Cardiomyopathies, Heart Diseases | Recruiting | 36 | — | — | |
| NCT06282432 Long-Term Follow-Up (LTFU) for Gene Therapy of Leukocyte Adhesion Deficiency-I (LAD-I) | Leukocyte Adhesion Deficiency | Active | 9 | — | — | |
| NCT06214507 Danon Disease Natural History Study | Danon Disease | Recruiting | 60 | — | — | |
| NCT04437771 Long-Term Follow-up of Subjects With Fanconi Anaemia Subtype A Treated With ex Vivo Gene Therapy | Fanconi Anemia Complementation Group A, Fanconi Anemia | Active | 9 | — | — | |
| NCT07369830 The Impact of Probiotic Intervention on the Gut Microbiota and Bowel Function | Rectal Cancer | N/A | Recruiting | 156 | RCT, Open-label | Clostridium butyricum (live) Tablets(Meiya) |
| NCT03831386 Gravity Versus Vacuum Based Indwelling Tunneled Pleural Drainage System | Pleural Effusion | N/A | Recruiting | 200 | RCT, Open-label | — |
| NCT07333053 Clinical Efficacy of Transarterial Infusion Chemotherapy for Unresectable Colorectal Cancer | Unresectable Colorectal Cancer | N/A | Recruiting | 30 | RCT, Open-label | — |
| NCT06662643 A Clinical Trial Comparing Staged Turnbull-Cutait Pull-through Anastomosis With Direct Anastomosis Plus Prophylactic Ileostomy in the Treatment of Low Rectal Cancer After Internal Sphincter Resection | Rectal Cancer, Rectal Carcinoma | N/A | Active | 110 | RCT, Single-blind | — |
| NCT02937974 Evaluate the Efficacy of Xuebijing Injection in Acute Exacerbations of COPD | Pulmonary Disease, Chronic Obstructive | P4 | Unknown | 254 | RCT, Double-blind | Xuebijing, Placebo |
| NCT07509398 FMT Combined With Standard First-Line Therapy in Initially Unresectable Colorectal Cancer | Unresectable Colorectal Cancer, Colorectal Cancer (Locally Advanced or Metastatic) | P2P3 | Not Yet Recruiting | 220 | RCT, Open-label | Standard First-Line Therapy |
| NCT06422351 Clinical Trial to Evaluate the Efficacy of Gene Therapy for Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency | P2 | SUSPENDED | 10 | Open-label | RP-L301 |
| NCT04069533 Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A | Fanconi Anemia Complementation Group A | P2 | Unknown | 7 | Open-label | RP-L102 |
| NCT03812263 A Clinical Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I | Leukocyte Adhesion Defect - Type I | P1P2 | Completed | 9 | Open-label | RP-L201 |
| NCT03825783 A Gene Therapy Trial to Evaluate the Safety and Efficacy of RP-L201 in Subjects With Leukocyte Adhesion Deficiency-I | Leukocyte Adhesion Defect - Type I | P1 | Withdrawn | — | Open-label | RP-L201 |
| NCT03882437 Gene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2B | Danon Disease | P1 | Unknown | 7 | Open-label | RP-A501 |
| NCT04525352 A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis | Infantile Malignant Osteopetrosis | P1 | Terminated | 1 | Open-label | RP-L401 |
| NCT03814408 A Clinical Trial to Evaluate the Safety of RP-L102 in Pediatric Subjects With Fanconi Anemia Subtype A | Fanconi Anemia Complementation Group A | P1 | Unknown | 2 | Open-label | RP-L102 |
| NCT04105166 Gene Therapy for Pyruvate Kinase Deficiency (PKD) | Pyruvate Kinase Deficiency | P1 | Completed | 4 | Open-label | RP-L301 |
| NCT01331018 Gene Therapy for Fanconi Anemia | Fanconi Anemia | P1 | Terminated | 3 | Open-label | Filgrastim, Genetically Engineered Hematopoietic Stem Progenitor Cells, Methylprednisolone, Plerixafor, Prednisone |
| NCT05548855 Natural History of Danon Disease | Danon Disease | Completed | 59 | — | — | |
| NCT07527975 Long-Term Follow-up: Phase I/II Clinical Study to Evaluate the Safety and Efficacy of the Infusion of RP-L102 | Fanconi Anemia | By Invite | 14 | — | RP-L102 | |
| NCT07486752 BAG3-DCM Natural History Study | Dilated Cardiomyopathy (DCM), Cardiovascular Diseases | Not Yet Recruiting | 30 | — | — | |
| NCT03766386 The Natural History of Danon Disease | Danon Disease | Unknown | 200 | — | — | |
| NCT03319186 EDIT Management Feasibility Trial | Pleural Effusion, Malignant | N/A | Unknown | 30 | RCT, Open-label | — |
| NCT04793607 Interventions for Malignant Pleural Effusions Impact on Fatigue | Malignant Pleural Effusion | Unknown | 50 | — | — | |
| NCT06082414 Systemic Management in Extremely Preterm and Extremely Low Birth Weight Infants | Bronchopulmonary Dysplasia, Death | Completed | 1,200 | — | — | |
| NCT03661801 Novel Pleural Fluid, Biopsy and Serum Biomarkers for the Investigation of Pleural Effusions | Respiratory Disease, Pleural Effusion | Completed | 313 | — | — | |
| NCT04967729 COVID-19 and Lung Ultrasound Utility | Covid19 | N/A | Completed | 26 | Open-label | — |
| NCT02805062 Manometry vs Clinical Assessment in the Detection of Trapped Lung in Patients With Suspected Pleural Malignancy | Pleural Effusion, Malignant | Unknown | 65 | — | — | |
| NCT03311165 Epidemiological Study of Neonatal Acute Respiratory Distress Syndrome (ARDS) | Neonatal Acute Respiratory Distress Syndrome(ARDS) | Completed | 1,000 | — | — | |
| NCT05727358 Effectiveness of Group Acceptance and Commitment Therapy in Treating Acute Stroke Patients With Depression | Acute Stroke Patients With Depression | N/A | Completed | 139 | RCT, Double-blind | — |